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Posters HCU Pegtibatinase

COMPOSE® Phase 1/2, dose-escalation Cohort 7 design: safety of pegtibatinase in children aged ≥5-<12 years with classical homocystinuria (HCU)

Events Metabolism HCU

Society for Inherited Metabolic Disorders (SIMD) Annual Meeting 2024

April 14 - 17, 2024

Charlotte

Events Metabolism HCU

Genetic Metabolic Dietitians International (GMDI) Annual Conference 2024

April 17 - 20, 2024

Charlotte

Events Metabolism HCU

Society for the Study of Inborn Errors of Metabolism (SSIEM) Symposium 2024

September 3 - 6, 2024

Porto