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Posters HCU

 Pegtibatinase, an Investigational Enzyme Replacement Therapy for the Treatment of Classical Homocystinuria (HCU): Latest Findings From the COMPOSE® Phase 1/2 Trial

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Posters HCU

SING: A Novel Tool for Dietary Management and Monitoring in Clinical Trials of Pegtibatinase, an Investigational Enzyme Replacement Therapy for Classical Homocystinuria

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Posters HCU

Novel Dietary Management Strategies for Classical Homocystinuria (HCU) in HARMONY/ENSEMBLE Phase 3 Studies of Pegtibatinase, an Investigational Enzyme Replacement Therapy

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Posters HCU

Latest Results From the COMPOSE® Phase 1/2 Trial for the Treatment of Classical Homocystinuria (HCU) Using Pegtibatinase, a Novel Investigational Enzyme Replacement Therapy

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Medical Information HCU

Pegtibatinase: The HARMONY/ENSEMBLE (Phase 3 Studies): Study Design

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Medical Information HCU

Classical Homocystinuria: Disease State and Treatment Options

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Medical Information HCU

Pegtibatinase: Mechanism of Action and Pharmacology

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Medical Information HCU

ACAPPELLA Study: Natural History Study of Classical HCU

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Posters HCU

Development of a Patient Identification Algorithm to Estimate Prevalence of Classical Homocystinuria (HCU) in the United States (US)

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Posters HCU

Insights From the First Genetic Evaluation of a Longitudinal Natural History Study in Classical Homocystinuria (HCU)

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Posters HCU

Population-based Incidence Estimates of Classical Homocystinuria Using the Genome Aggregation Database (gnomAD)

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Abstracts HCU

Validation of a patient identification algorithm to estimate the prevalence of classical homocystinuria (HCU) in the United States (US)

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Abstracts HCU

Clinical burden of classical homocystinuria in the United States: a retrospective analysis of Optum Market Clarity

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