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Posters HCU

 Pegtibatinase, an Investigational Enzyme Replacement Therapy for the Treatment of Classical Homocystinuria (HCU): Latest Findings From the COMPOSE® Phase 1/2 Trial

Posters HCU

SING: A Novel Tool for Dietary Management and Monitoring in Clinical Trials of Pegtibatinase, an Investigational Enzyme Replacement Therapy for Classical Homocystinuria

Posters HCU

Novel Dietary Management Strategies for Classical Homocystinuria (HCU) in HARMONY/ENSEMBLE Phase 3 Studies of Pegtibatinase, an Investigational Enzyme Replacement Therapy

Posters HCU

Latest Results From the COMPOSE® Phase 1/2 Trial for the Treatment of Classical Homocystinuria (HCU) Using Pegtibatinase, a Novel Investigational Enzyme Replacement Therapy

Medical Information HCU

Pegtibatinase: The HARMONY/ENSEMBLE (Phase 3 Studies): Study Design

Medical Information HCU

Classical Homocystinuria: Disease State and Treatment Options

Medical Information HCU

Pegtibatinase: Mechanism of Action and Pharmacology

Medical Information HCU

ACAPPELLA Study: Natural History Study of Classical HCU

Posters HCU

Development of a Patient Identification Algorithm to Estimate Prevalence of Classical Homocystinuria (HCU) in the United States (US)

Posters HCU

Insights From the First Genetic Evaluation of a Longitudinal Natural History Study in Classical Homocystinuria (HCU)

Posters HCU

Population-based Incidence Estimates of Classical Homocystinuria Using the Genome Aggregation Database (gnomAD)

Abstracts HCU

Validation of a patient identification algorithm to estimate the prevalence of classical homocystinuria (HCU) in the United States (US)

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Abstracts HCU

Clinical burden of classical homocystinuria in the United States: a retrospective analysis of Optum Market Clarity

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