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Abstracts HCU

Pegtibatinase, an Investigational Enzyme Replacement Therapy for the Treatment of Classical Homocystinuria: Initial Results from the Phase 1/2 Compose Study

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Posters HCU

Pegtibatinase and Initial Results from the COMPOSE Clinical Trial for Classical HCU

Posters HCU

Pegtibatinase, an Investigational Enzyme Replacement Therapy for the Treatment of Classical Homocystinuria: Initial Results From the Phase 1/2 COMPOSE Study

Posters HCU

Pegtibatinase, an Investigational Enzyme Replacement Therapy for the Treatment of Classical Homocystinuria: Initial Results from the Phase 1/2 COMPOSE Study

Abstracts HCU

Dietary Goals and Current Challenges in the Management of Classical Homocystinuria: Insights From Multinational Real-World Experience

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Posters HCU

Dietary Goals and Current Challenges in the Management of Classical Homocystinuria: Insights From Multinational Real-World Experience

Publications HCU

Accurate 24‐h urine cystine quantification for patients on cystine‐binding thiol drugs

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Publications HCU

Assessment of health‐related quality of life in patients with cystinuria on tiopronin therapy

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