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Abstracts HCU

“Development of a Patient Identification Algorithm to Estimate Prevalence of Classical Homocystinuria in the United States (US)

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Abstracts HCU

Insights from the First Genetic Evaluation of a Longitudinal Natural History Study in Classical Homocystinuria (HCU)

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Abstracts HCU

Population-Based Incidence Estimates of Classical Homocystinuria Using the Genome Aggregation Database (gnomAD)

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Posters HCU

Population-based Incidence Estimates of Classical Homocystinuria Using the Genome Aggregation Database (gnomAD)

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Posters HCU

A Longitudinal Study of Cognitive Function in Classical Homocystinuria (HCU) Demonstrates Distinct Deficits in Inhibitory Control

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Posters HCU

Insights from the First Genetic Evaluation of a Longitudinal Natural History Study in Classical Homocystinuria (HCU)

Learn More
Posters HCU

Population-based Incidence Estimates of Classical Homocystinuria Using the Genome Aggregation Database (gnomAD)

Learn More
Posters HCU

A Longitudinal Study of Cognitive Function in Classical Homocystinuria (HCU) Demonstrates Distinct Deficits in Inhibitory Control

Learn More
Posters HCU

Insights from the First Genetic Evaluation of a Longitudinal Natural History Study in Classical Homocystinuria (HCU)

Learn More
Abstracts HCU

Insights from the First Genetic Evaluation of a Longitudinal Natural History Study in Classical Homocystinuria (HCU)

View
Abstracts HCU

Population-based incidence estimates of classical homocystinuria using the Genome Aggregation Database (gnomAD)

View
Abstracts HCU

A Longitudinal Study of Cognitive Function in Classical Homocystinuria Demonstrates Distinct Deficits in Inhibitory Control

View
Abstracts HCU

Pegtibatinase, an Investigational Enzyme Replacement Therapy for the Treatment of Classical Homocystinuria: Initial Results from the Phase 1/2 Compose Study

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